WEP Clinical (WEP) is pleased to announce our partnership with Pharming Group N.V. (“Pharming” EURONEXT Amsterdam: PHARM/Nasdaq: PHAR), a specialty pharmaceutical company developing innovative products for the safe, effective treatment of rare diseases and unmet medical needs, to make rare disease investigational drug, leniolisib, available through an Expanded Access Program (EAP).
Leniolisib is being developed to treat Activated PI3K Delta Syndrome (APDS). APDS is defined as a rare, genetic, primary immunodeficiency disease with a prevalence of 1 – 2 per 1,000,000 of population and characterised by increased susceptibility to recurrent and/or severe bacterial and viral infections, chronic benign lymphoproliferation, and/or autoimmune disease and premature mortality. Leniolisib was recently in-licensed by Pharming from Novartis and is being studied in a registration-enabling Phase II/III trial.
Together, Pharming and WEP transitioned patients from the previous Novartis-run EAP into the Pharming EAP, managed by WEP, to allow patients to continue accessing the treatment.
The objective of this EAP is to provide leniolisib to eligible APDS patients in need of treatment who are otherwise unable to participate in a clinical study or for whom access is otherwise not available through marketed product in their country, and to provide physicians with early access and experience with leniolisib.
Jas Khera, Managing Director of WEP, said:
“It is great to be working with Pharming to support making this drug available to patients diagnosed with APDS. This EAP will ensure that patients with a high unmet need have a secure and compliant supply of this treatment option available to them, which is in-keeping with WEP’s and Pharming’s shared goal of broadening access to critical, innovative medicines worldwide.”
Health care professionals can inquire for more details about leniolisib and the EAP by emailing WEP at leeap@wepclinical.com
About WEP
At WEP Clinical, we are With Every Patient, as we believe every patient should have access to treatment! With this as our leading principle, we have created a market leading, solutions driven, healthcare services company that partners with drug developers to create broader treatment access for patients worldwide. We take pride in the high-quality output and positive customer experience we create while delivering our services. We specialize in the following: Expanded Access and Post-Approval Named Patient Programs; Market Access Solutions; Home Nursing Services for Decentralized Clinical Trials; and Clinical Trial Sourcing. For more information, please visit www.wepclinical.com.
About Pharming
Pharming Group N.V. (EURONEXT Amsterdam: PHARM/Nasdaq: PHAR) is a global biopharmaceutical company dedicated to transforming the lives of patients with rare, debilitating, and life-threatening diseases. Pharming is commercialising and developing an innovative portfolio of protein replacement therapies and precision medicines, including small molecules, biologics, and gene therapies that are in early to late-stage development. Pharming is headquartered in Leiden, Netherlands, and has employees around the globe who serve patients in over 30 markets in North America, Europe, the Middle East, Africa, and Asia-Pacific. For more information, visit www.pharming.com
